RecruitingPrion Disease
PrP-targeting siRNA Safety & Mechanism Study
Eligible age
18+ yrs
Accepts
All genders
Locations
5 states
Healthy volunteers
No
See if you qualify for this study
Answer a few quick questions about your location and health. Takes about a minute.
About this study
The purpose of this trial is to evaluate safety, tolerability, pharmacokinetics and pharmacodynamic impact of PrP-siRNA in symptomatic prion disease patients.
Sponsor: Broad Institute of MIT and Harvard
Where it's recruiting
Source: ClinicalTrials.gov · NCT07444580 · last updated 2026-06-05