RecruitingFabry Disease
A Study of Patients With Fabry Disease (US Specific)
Eligible age
18+ yrs
Accepts
All genders
Locations
8 states
Healthy volunteers
No
See if you qualify for this study
Answer a few quick questions about your location and health. Takes about a minute.
About this study
This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.
Sponsor: Amicus Therapeutics
You may not qualify if…
- ✕ 1\. Patients who currently are participating in a clinical trial of any investigational medicinal product or device at the time of enrollment
Where it's recruiting
Source: ClinicalTrials.gov · NCT06906367 · last updated 2026-07-10